X-linked severe combined immunodeficiency

Results: 55



#Item
11Transplantation medicine / X-linked severe combined immunodeficiency / Severe combined immunodeficiency / Gene therapy / Janus kinase 3 / Allotransplantation / Medicine / Biology / Health

Protocol #[removed]: Gene Therapy for SCID-X1 Using a Self-Inactivating (SIN) Gammaretrovirus Luigi Notarangelo, M.D. PI, Children’s Hospital Boston Site

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2014-01-06 11:40:34
12Medicine / Health / Viral vector / Retrovirus / Vector / Severe combined immunodeficiency / Biotechnology / National Institutes of Health / X-linked severe combined immunodeficiency / Biology / Gene delivery / Molecular biology

Gene Transfer Clinical Trials Using Retroviral Vectors Gene Transfer Clinical Trials

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-10 13:22:13
13Mathematics / Molecular biology / Viral vector / X-linked severe combined immunodeficiency / Retrovirus / Common gamma chain / Vector space / Vector / Severe combined immunodeficiency / Algebra / Biology / Gene delivery

Protocol #[removed]Gene transfer for SCID-X1 using a selfinactivating (SIN) gammaretroviral vector Presentation to Recombinant DNA Advisory Committee Luigi D. Notarangelo MD (PI) Sung-Yun Pai MD (co-I) David A. Williams

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-31 11:54:39
14Rare diseases / Transplantation medicine / Lymphocytes / Severe combined immunodeficiency / X-linked severe combined immunodeficiency / Cytokine receptors / Janus kinase 3 / Graft-versus-host disease / Common gamma chain / Medicine / Health / Biology

Recombinant Advisory Committee Meeting December 4, 2008 • Update on Bone Marrow Transplantation for X-linked Severe Combined Immunodeficiency (X-SCID) at Duke University Medical Center

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2014-01-06 11:40:07
15Gene delivery / Rare diseases / Emerging technologies / Bioethics / Medical research / Severe combined immunodeficiency / Gene therapy / Adenosine deaminase / X-linked severe combined immunodeficiency / Biology / Health / Medicine

Microsoft PowerPoint - EFS-ADA_RAC120209.ppt

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2014-01-06 12:15:58
16Biotechnology / Rare diseases / Molecular biology / Bioethics / Gene therapy / Health and Social Care Survey / Adenosine deaminase deficiency / X-linked severe combined immunodeficiency / Biology / Health / Medicine

Severe Combined Immunodeficiencies Unknown (7% Reticular Dysgenesi (<1%)

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-16 10:00:06
17Biotechnology / Emerging technologies / Medical research / Gene therapy / Severe combined immunodeficiency / X-linked severe combined immunodeficiency / Viral vector / CD34 / Hematopoietic stem cell / Biology / Gene delivery / Molecular biology

Review of Selected ASGT Annual Meeting Sessions related to Retroviral Vectors z Hematopoietic Marking Studies

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2014-01-14 10:39:13
18Viral vector / Retrovirus / Severe combined immunodeficiency / X-linked severe combined immunodeficiency / Vector / Virus / Vectors in Gene Therapy / Biology / Gene delivery / Molecular biology

Informed Consents for Clinical T i l Using Trials U i Integrating I i Vectors

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-10 13:18:12
19Biotechnology / Severe combined immunodeficiency / Viral vector / X-linked severe combined immunodeficiency / Stem cell / Retrovirus / Vector / Gene therapy / Biology / Gene delivery / Molecular biology

Gene Transfer for X-SCID: Conclusions and Recommendations of the RAC March 3, 2009 Previous RAC Gene Transfer Safety Symposia:

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2014-01-06 12:50:46
20Hematology / Rare diseases / Gene delivery / Hematopoietic stem cell / CD34 / Severe combined immunodeficiency / Gene therapy / Intravenous immunoglobulin / Apheresis / Biology / Medicine / Stem cells

GENE THERAPY IN TWO PRE-ADOLESCENTS WITH X-LINKED SEVERE COMBINED IMMUNODEFICIENCY (XSCID)

Add to Reading List

Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-16 09:47:08
UPDATE